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In Vivo RNA Delivery to Hematopoietic Stem and Progenitor Cells via Targeted Lipid Nanoparticles

https://doi.org/10.1021/acs.nanolett.3c00304
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What this work says

Outgoing claims: the papers this work cites, builds on, or argues with.

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Hematopoietic Stem Cell Gene Therapy: Progress and Lessons Learned
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In Vivo HSC Gene Therapy Using a Bi-modular HDAd5/35++ Vector Cures Sickle Cell Disease in a Mouse Model
inferredcites →https://doi.org/10.1016/j.ymthe.2020.11.020openalex-snapshot
Update on Clinical Ex Vivo Hematopoietic Stem Cell Gene Therapy for Inherited Monogenic Diseases
inferredcites →https://doi.org/10.1016/j.ymthe.2022.06.012openalex-snapshot
Lipid nanoparticle-mediated silencing of osteogenic suppressor GNAS leads to osteogenic differentiation of mesenchymal stem cells in vivo
inferredcites →https://doi.org/10.1021/jacs.8b08976openalex-snapshot
Nanoparticles That Deliver RNA to Bone Marrow Identified by in Vivo Directed Evolution
inferredcites →https://doi.org/10.1038/mtna.2013.66openalex-snapshot
Influence of Polyethylene Glycol Lipid Desorption Rates on Pharmacokinetics and Pharmacodynamics of siRNA Lipid Nanoparticles
inferredcites →https://doi.org/10.1038/nature25022openalex-snapshot
From haematopoietic stem cells to complex differentiation landscapes
inferredcites →https://doi.org/10.1038/nn.2467openalex-snapshot
A robust and high-throughput Cre reporting and characterization system for the whole mouse brain
inferredcites →https://doi.org/10.1038/pr.2011.57openalex-snapshot
Complications of autologous hematopoietic stem cell transplantation for patients with autoimmune diseases
inferredcites →https://doi.org/10.1038/s41375-020-0818-9openalex-snapshot
Anti-human CD117 CAR T-cells efficiently eliminate healthy and malignant CD117-expressing hematopoietic cells
inferredcites →https://doi.org/10.1038/s41467-018-08201-xopenalex-snapshot
Selective hematopoietic stem cell ablation using CD117-antibody-drug-conjugates enables safe and effective transplantation with immunity preservation
inferredcites →https://doi.org/10.1038/s41551-020-00623-7openalex-snapshot
Nanoparticle-encapsulated siRNAs for gene silencing in the haematopoietic stem-cell niche
inferredcites →https://doi.org/10.1038/s41576-020-00298-5openalex-snapshot
Gene therapy using haematopoietic stem and progenitor cells
inferredcites →https://doi.org/10.1038/s41577-022-00698-0openalex-snapshot
Immunological barriers to haematopoietic stem cell gene therapy
inferredcites →https://doi.org/10.1038/s41586-019-1711-4openalex-snapshot
Search-and-replace genome editing without double-strand breaks or donor DNA
inferredcites →https://doi.org/10.1038/s41586-021-03609-wopenalex-snapshot
Base editing of haematopoietic stem cells rescues sickle cell disease in mice
inferredcites →https://doi.org/10.1038/s41591-022-01934-9openalex-snapshot
Ensuring a future for gene therapy for rare diseases
inferredcites →https://doi.org/10.1038/srep05199openalex-snapshot
Dynamic equilibrium of heterogeneous and interconvertible multipotent hematopoietic cell subsets
inferredcites →https://doi.org/10.1056/nejmoa2027675openalex-snapshot
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency
inferredcites →https://doi.org/10.1056/nejmoa2031054openalex-snapshot
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia
inferredcites →https://doi.org/10.1056/nejmoa2106596openalex-snapshot
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome
inferredcites →https://doi.org/10.1126/scitranslmed.aae0501openalex-snapshot
Hematopoietic stem cell transplantation in immunocompetent hosts without radiation or chemotherapy
inferredcites →https://doi.org/10.1152/physrev.00046.2011openalex-snapshot
Stem Cell Factor Receptor/c-Kit: From Basic Science to Clinical Implications
inferredcites →https://doi.org/10.1172/jci122836openalex-snapshot
In vivo hematopoietic stem cell gene therapy ameliorates murine thalassemia intermedia
inferredcites →https://doi.org/10.1182/bloodadvances.2020003702openalex-snapshot
In vivo HSPC gene therapy with base editors allows for efficient reactivation of fetal γ-globin in β-YAC mice
inferredcites →https://doi.org/10.3389/fimmu.2021.736692openalex-snapshot
Mast Cells Are Identified in the Lung Parenchyma of Wild Mice, Which Can Be Recapitulated in Naturalized Laboratory Mice

What points at this work

Incoming claims: where this work appears in other papers’ reference lists and arguments.

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inferred← citeshttps://doi.org/10.1208/s12248-023-00860-zopenalex-snapshot
RNA Nanomedicine: Delivery Strategies and Applications
inferred← citeshttps://doi.org/10.1360/tb-2023-0613openalex-snapshot
Recent advances in strategies for developing tissue-selective mRNA-LNP technology
inferred← citeshttps://doi.org/10.17925/ohr.2023.19.2.29openalex-snapshot
Cell-based Genetic Therapy for the Induction of Foetal Haemoglobin in Sickle Cell Disease and Transfusion-dependent β-thalassaemia
inferred← citeshttps://doi.org/10.20517/rdodj.2025.42openalex-snapshot
Gene therapy for inborn errors of immunity: past progress, current status and future directions
inferred← citeshttps://doi.org/10.2147/ijn.s598126openalex-snapshot
Nanoparticle Drug Delivery Systems: The Future Direction for the Treatment of Tumors
inferred← citeshttps://doi.org/10.25259/jhas_5_2024openalex-snapshot
RNA therapeutics in hematology
inferred← citeshttps://doi.org/10.26599/nr.2025.94907422openalex-snapshot
Unlocking the full therapeutic potential of lipid nanoparticles through extrahepatic delivery
inferred← citeshttps://doi.org/10.3389/fgeed.2023.1148693openalex-snapshot
Current approaches and potential challenges in the delivery of gene editing cargos into hematopoietic stem and progenitor cells
inferred← citeshttps://doi.org/10.3389/fimmu.2025.1653344openalex-snapshot
Next generation targeted non-genotoxic conditioning for hematopoietic stem cell and hematopoietic stem cell-based gene therapy
inferred← citeshttps://doi.org/10.3389/fonc.2026.1874395openalex-snapshot
Antigen-directed p53 restoration in TP53-mutated myeloid neoplasms: a hypothesis and theory perspective
inferred← citeshttps://doi.org/10.3390/biology15181657openalex-snapshot
PU.1 as a Master Regulator of Immune Cell Development and Function: Structural Basis, Gene Regulatory Networks, Disease Roles, and Therapeutic Targeting
inferred← citeshttps://doi.org/10.3390/biomedicines13030758openalex-snapshot
Scientific Advancements in Gene Therapies: Opportunities for Global Regulatory Convergence
inferred← citeshttps://doi.org/10.3390/cells14201595openalex-snapshot
Advances in β-Thalassemia Gene Therapy: CRISPR/Cas Systems and Delivery Innovations
inferred← citeshttps://doi.org/10.3390/ijms242015230openalex-snapshot
RNA-Based Therapeutic Technology
inferred← citeshttps://doi.org/10.3390/ijms25010658openalex-snapshot
The Current Situation and Development Prospect of Whole-Genome Screening
inferred← citeshttps://doi.org/10.3390/ijms26051814openalex-snapshot
Nanotherapy of Glioblastoma—Where Hope Grows
inferred← citeshttps://doi.org/10.3390/ijms27031203openalex-snapshot
miRNA-Mediated Regulation of γ-Globin to β-Globin Switching: Therapeutic Potential in β-Hemoglobinopathies
inferred← citeshttps://doi.org/10.3390/vaccines12020186openalex-snapshot
Lipid Nanoparticle (LNP) Delivery Carrier-Assisted Targeted Controlled Release mRNA Vaccines in Tumor Immunity
inferred← citeshttps://doi.org/10.34133/research.0370openalex-snapshot
Unlocking the Therapeutic Applicability of LNP-mRNA: Chemistry, Formulation, and Clinical Strategies
inferred← citeshttps://doi.org/10.52601/bpr.2023.230022openalex-snapshot
Surface engineering of lipid nanoparticles: targeted nucleic acid delivery and beyond
inferred← citeshttps://doi.org/10.5599/admet.2160openalex-snapshot
Frontiers of stem cell engineering for nanotechnology-mediated drug delivery systems
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