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Manufacturing and characterizing AAV-based vectors for use in clinical studies
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What this work says
Outgoing claims: the papers this work cites, builds on, or argues with.
inferredcites →https://doi.org/10.1002/jgm.1092openalex-snapshot
Economized large‐scale production of high yield of rAAV for gene therapy applications exploiting baculovirus expression system
inferredcites →https://doi.org/10.1007/978-3-642-75608-5_5openalex-snapshot
Use of Adeno-Associated Virus as a General Transduction Vector for Mammalian Cells
inferredcites →https://doi.org/10.1007/s00439-006-0165-6openalex-snapshot
Treatment of human disease by adeno-associated viral gene transfer
inferredcites →https://doi.org/10.1016/j.expneurol.2007.08.009openalex-snapshot
Current status of gene therapy trials for Parkinson's disease
inferredcites →https://doi.org/10.1016/j.jviromet.2003.09.002openalex-snapshot
Serum-free production and column purification of adeno-associated virus type 5
inferredcites →https://doi.org/10.1016/j.jviromet.2004.07.001openalex-snapshot
Purification of recombinant adeno-associated virus type 8 vectors by ion exchange chromatography generates clinical grade vector stock
inferredcites →https://doi.org/10.1016/j.jviromet.2006.11.019openalex-snapshot
Separation of adeno-associated virus type 2 empty particles from genome containing vectors by anion-exchange column chromatography
inferredcites →https://doi.org/10.1016/j.ymthe.2004.08.030openalex-snapshot
Herpesvirus-based infectious titering of recombinant adeno-associated viral vectors
inferredcites →https://doi.org/10.1016/j.ymthe.2005.02.021openalex-snapshot
Identification of factors that contribute to recombinant AAV2 particle aggregation and methods to prevent its occurrence during vector purification and formulation
inferredcites →https://doi.org/10.1016/j.ymthe.2005.06.003openalex-snapshot
Evidence for Encapsidation of Prokaryotic Sequences during Recombinant Adeno-Associated Virus Production and Their in Vivo Persistence after Vector Delivery
inferredcites →https://doi.org/10.1016/s0076-6879(02)46069-7openalex-snapshot
[24] Streamlined large-scale production of recombinant adeno-associated virus (rAAV) vectors
inferredcites →https://doi.org/10.1016/s0958-1669(02)00369-5openalex-snapshot
Production of clinical-grade recombinant adeno-associated virus vectors
inferredcites →https://doi.org/10.1016/s1525-0016(02)00019-9openalex-snapshot
Quantification of adeno-associated virus particles and empty capsids by optical density measurement
inferredcites →https://doi.org/10.1016/s1525-0016(02)90719-7openalex-snapshot
A Versatile and Scalable Two-Step Ion-Exchange Chromatography Process for the Purification of Recombinant Adeno-associated Virus Serotypes-2 and -5
inferredcites →https://doi.org/10.1016/s1525-0016(16)41342-0openalex-snapshot
900. Packaging of Host Cell and Plasmid DNA into Recombinant Adeno-Associated Virus Particles Produced by Triple Transfection
inferredcites →https://doi.org/10.1016/s1525-0016(16)41455-3openalex-snapshot
1013. In Vivo Performance of AAV2 Vectors Purified by CsCl Gradient Centrifugation or Column Chromatography
inferredcites →https://doi.org/10.1016/s1525-0016(16)44927-0openalex-snapshot
721. Intravenous Injection Cofactors of Adeno-Associated Virus Produce Varying Tissue-Specific Transduction Levels in Adult Mice
inferredcites →https://doi.org/10.1038/nm1358openalex-snapshot
Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response
inferredcites →https://doi.org/10.1038/nm1549openalex-snapshot
CD8+ T-cell responses to adeno-associated virus capsid in humans
inferredcites →https://doi.org/10.1038/sj.gt.3300680openalex-snapshot
Adeno-associated virus vectors can be efficiently produced without helper virus
inferredcites →https://doi.org/10.1038/sj.gt.3300937openalex-snapshot
High-titer recombinant adeno-associated virus production utilizing a recombinant herpes simplex virus type I vector expressing AAV-2 Rep and Cap
inferredcites →https://doi.org/10.1038/sj.gt.3300938openalex-snapshot
Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield
inferredcites →https://doi.org/10.1038/sj.mt.6300389openalex-snapshot
Reversal of Blindness in Animal Models of Leber Congenital Amaurosis Using Optimized AAV2-mediated Gene Transfer
inferredcites →https://doi.org/10.1074/jbc.m101559200openalex-snapshot
Binding of Adeno-associated Virus Type 5 to 2,3-Linked Sialic Acid Is Required for Gene Transfer
inferredcites →https://doi.org/10.1089/104303400750001390openalex-snapshot
Purification of Recombinant Adeno-Associated Virus Vectors by Column Chromatography and Its Performance in Vivo
inferredcites →https://doi.org/10.1089/104303402320139014openalex-snapshot
Scalable Purification of Adeno-Associated Virus Type 2, 4, or 5 Using Ion-Exchange Chromatography
inferredcites →https://doi.org/10.1089/10430340260355347openalex-snapshot
Insect Cells as a Factory to Produce Adeno-Associated Virus Type 2 Vectors
inferredcites →https://doi.org/10.1089/1043034041361262openalex-snapshot
Infectious Titer Assay for Adeno-Associated Virus Vectors with Sensitivity Sufficient to Detect Single Infectious Events
inferredcites →https://doi.org/10.1089/10430349950018427openalex-snapshot
Highly Purified Recombinant Adeno-Associated Virus Vectors Are Biologically Active and Free of Detectable Helper and Wild-Type Viruses
inferredcites →https://doi.org/10.1089/hum.1995.6.10-1329openalex-snapshot
Cell Lines for the Production of Recombinant Adeno-Associated Virus
inferredcites →https://doi.org/10.1089/hum.1998.9.18-2745openalex-snapshot
Novel Tools for Production and Purification of Recombinant Adenoassociated Virus Vectors
inferredcites →https://doi.org/10.1089/hum.2005.16.541openalex-snapshot
Adeno-Associated Virus Vectors in Clinical Trials
inferredcites →https://doi.org/10.1128/jvi.61.10.3096-3101.1987openalex-snapshot
A recombinant plasmid from which an infectious adeno-associated virus genome can be excised in vitro and its use to study viral replication
inferredcites →https://doi.org/10.1128/jvi.63.9.3822-3828.1989openalex-snapshot
Helper-free stocks of recombinant adeno-associated viruses: normal integration does not require viral gene expression
inferredcites →https://doi.org/10.1128/jvi.71.9.6816-6822.1997openalex-snapshot
Identification and elimination of replication-competent adeno-associated virus (AAV) that can arise by nonhomologous recombination during AAV vector production
inferredcites →https://doi.org/10.1128/jvi.72.1.309-319.1998openalex-snapshot
Infectious Clones and Vectors Derived from Adeno-Associated Virus (AAV) Serotypes Other Than AAV Type 2
inferredcites →https://doi.org/10.1128/jvi.72.2.1438-1445.1998openalex-snapshot
Membrane-Associated Heparan Sulfate Proteoglycan Is a Receptor for Adeno-Associated Virus Type 2 Virions
inferredcites →https://doi.org/10.1128/jvi.72.3.2224-2232.1998openalex-snapshot
Production of High-Titer Recombinant Adeno-Associated Virus Vectors in the Absence of Helper Adenovirus
inferredcites →https://doi.org/10.1128/jvi.73.2.1309-1319.1999openalex-snapshot
Cloning and Characterization of Adeno-Associated Virus Type 5
inferredcites →https://doi.org/10.1182/blood-2007-05-091363openalex-snapshot
What for platelet factor 4?
inferredcites →https://doi.org/10.1182/blood.v110.11.3736.3736openalex-snapshot
Trace Capsid DNA Impurities in AAV2 Vectors Are Not Transcribed and Are Unlikely To Contribute to Capsid Peptide-MHC Class I Complexes
inferredcites →https://doi.org/10.1182/blood.v110.11.3737.3737openalex-snapshot
Quantifying Capsid Peptide:MHC I Complexes Following Adeno-Associated Virus (AAV) Transduction
inferredcites →https://doi.org/10.1289/ehp.114-a556aopenalex-snapshot
The Cutter Incident: How America’s First Polio Vaccine Led to the Growing Vaccine Crisis
inferredcites →https://doi.org/10.4049/jimmunol.166.12.7268openalex-snapshot
Factors Affecting the Efficiency of CD8+ T Cell Cross-Priming with Exogenous Antigens
inferredcites →https://doi.org/10.5281/zenodo.8192864openalex-snapshot
GUIDANCE FOR INDUSTRY QUALITY SYSTEMS APPROACH TO PHARMACEUTICAL CGMP REGULATIONS
inferredcites →https://doi.org/10.5860/choice.43-2842openalex-snapshot
The Cutter incident: how America's first polio vaccine led to the growing vaccine crisis
What points at this work
Incoming claims: where this work appears in other papers’ reference lists and arguments.
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Adeno-Associated Virus Analysis by Size Exclusion Chromatography within 3 Minutes Using Short Bio-Inert Columns Made with 3 Μm Particles Operated at High Flowrates
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Chromatography in Downstream Processing of Recombinant Adeno‐Associated Viruses: A Review of Current and Future Practises
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Enrichment of Full AAV2 Using Multicolumn Countercurrent Solvent Gradient Purification (MCSGP)
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Cell and Gene Therapies Manufacturing Challenges and Integrated Good Manufacturing Practices Solutions: A Lifecycle Perspective
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Multi‐omics kinetic analysis of recombinant adeno‐associated virus production by plasmid transfection of HEK293 cells
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MicroRNA‐based recombinant AAV vector assembly improves efficiency of suicide gene transfer in a murine model of lymphoma
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Clinical practice guidelines for gene therapy to treat hereditary hearing loss
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Utilizing adeno‐associated virus as a vector in treating genetic disorders or human cancers
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DNA Released by Adeno-Associated Virus Strongly Alters Capsid Aggregation Kinetics in a Physiological Solution
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Differentially Branched Ester Amine Quadpolymers with Amphiphilic and pH-Sensitive Properties for Efficient Plasmid DNA Delivery
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Surface Modified Nano-Electrospray Needles Improve Sensitivity for Native Mass Spectrometry
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inferred← citeshttps://doi.org/10.1038/gt.2009.23openalex-snapshot
AAV for pain: steps towards clinical translation
inferred← citeshttps://doi.org/10.1038/mt.2008.227openalex-snapshot
Undetectable Transcription of cap in a Clinical AAV Vector: Implications for Preformed Capsid in Immune Responses
inferred← citeshttps://doi.org/10.1038/mt.2010.274openalex-snapshot
Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins
inferred← citeshttps://doi.org/10.1038/mt.2016.62openalex-snapshot
Pulmonary Targeting of Adeno-associated Viral Vectors by Next-generation Sequencing-guided Screening of Random Capsid Displayed Peptide Libraries
inferred← citeshttps://doi.org/10.1038/mtm.2016.2openalex-snapshot
Manufacturing of recombinant adeno-associated viral vectors for clinical trials
inferred← citeshttps://doi.org/10.1038/mtm.2016.6openalex-snapshot
The impact of minimally oversized adeno-associated viral vectors encoding human factor VIII on vector potency in vivo
inferred← citeshttps://doi.org/10.1038/mtna.2016.60openalex-snapshot
DNA Minicircle Technology Improves Purity of Adeno-associated Viral Vector Preparations
inferred← citeshttps://doi.org/10.1038/nrg2988openalex-snapshot
Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges
inferred← citeshttps://doi.org/10.1038/s41392-024-01780-wopenalex-snapshot
Adeno-associated virus as a delivery vector for gene therapy of human diseases
inferred← citeshttps://doi.org/10.1038/s41587-022-01418-8openalex-snapshot
High-yield genome engineering in primary cells using a hybrid ssDNA repair template and small-molecule cocktails
inferred← citeshttps://doi.org/10.1039/d0tb00321bopenalex-snapshot
Macrocyclic polyamine [12]aneN 3 modified triphenylamine-pyrazine derivatives as efficient non-viral gene vectors with AIE and two-photon imaging properties
inferred← citeshttps://doi.org/10.1039/d2nr06401dopenalex-snapshot
Microfluidic production of nanogels as alternative triple transfection reagents for the manufacture of adeno-associated virus vectors
inferred← citeshttps://doi.org/10.1080/10408363.2019.1633512openalex-snapshot
Production of CAR T-cells by GMP-grade lentiviral vectors: latest advances and future prospects
inferred← citeshttps://doi.org/10.1080/14712598.2020.1693541openalex-snapshot
Current challenges in biotherapeutic particles manufacturing
inferred← citeshttps://doi.org/10.1089/apb.2021.0020openalex-snapshot
A Changing World in Gene Therapy Research: Exciting Opportunities for Medical Advancement and Biosafety Challenges
inferred← citeshttps://doi.org/10.1089/biores.2020.0031openalex-snapshot
Two-Plasmid Packaging System for Recombinant Adeno-Associated Virus
inferred← citeshttps://doi.org/10.1089/hgtb.2012.049openalex-snapshot
Quantification of AAV Particle Titers by Infrared Fluorescence Scanning of Coomassie-Stained Sodium Dodecyl Sulfate–Polyacrylamide Gels
inferred← citeshttps://doi.org/10.1089/hgtb.2016.026openalex-snapshot
Optimization of Internally Deleted Dystrophin Constructs
inferred← citeshttps://doi.org/10.1089/hgtb.2016.124openalex-snapshot
Characteristics of Minimally Oversized Adeno-Associated Virus Vectors Encoding Human Factor VIII Generated Using Producer Cell Lines and Triple Transfection
inferred← citeshttps://doi.org/10.1089/hgtb.2016.185openalex-snapshot
Accurate Identification and Quantification of DNA Species by Next-Generation Sequencing in Adeno-Associated Viral Vectors Produced in Insect Cells
inferred← citeshttps://doi.org/10.1089/hgtb.2017.246openalex-snapshot
In Vivo Potency Assay for Adeno-Associated Virus–Based Gene Therapy Vectors Using AAVrh.10 as an Example
inferred← citeshttps://doi.org/10.1089/hum.2009.064openalex-snapshot
Transient Transfection Methods for Clinical Adeno-Associated Viral Vector Production
inferred← citeshttps://doi.org/10.1089/hum.2009.125openalex-snapshot
Adenovirus–Adeno-Associated Virus Hybrid for Large-Scale Recombinant Adeno-Associated Virus Production
inferred← citeshttps://doi.org/10.1089/hum.2010.129openalex-snapshot
Evaluation and Optimization of the Administration of Recombinant Adeno-Associated Viral Vectors (Serotypes 2/1, 2/2, 2/rh8, 2/9, and 2/rh10) by Convection-Enhanced Delivery to the Striatum
inferred← citeshttps://doi.org/10.1089/hum.2015.050openalex-snapshot
OneBac 2.0: Sf 9 Cell Lines for Production of AAV5 Vectors with Enhanced Infectivity and Minimal Encapsidation of Foreign DNA
inferred← citeshttps://doi.org/10.1089/hum.2016.160openalex-snapshot
Adeno-Associated Virus Gene Therapy for Liver Disease
inferred← citeshttps://doi.org/10.1089/hum.2019.284openalex-snapshot
Single-Use Capture Purification of Adeno-Associated Viral Gene Transfer Vectors by Membrane-Based Steric Exclusion Chromatography
inferred← citeshttps://doi.org/10.1089/hum.2021.009openalex-snapshot
Characterization of Adeno-Associated Virus Capsid Proteins with Two Types of VP3-Related Components by Capillary Gel Electrophoresis and Mass Spectrometry
inferred← citeshttps://doi.org/10.1089/hum.2021.123openalex-snapshot
Size Exclusion Chromatography with Dual Wavelength Detection as a Sensitive and Accurate Method for Determining the Empty and Full Capsids of Recombinant Adeno-Associated Viral Vectors
inferred← citeshttps://doi.org/10.1089/hum.2021.182openalex-snapshot
Insight and Development of Advanced Recombinant Adeno-Associated Virus Analysis Tools Exploiting Single-Particle Quantification by Multidimensional Droplet Digital PCR
inferred← citeshttps://doi.org/10.1089/humc.2015.006openalex-snapshot
Duchenne Muscular Dystrophy Gene Therapy in the Canine Model
inferred← citeshttps://doi.org/10.1093/ckj/sfaf332openalex-snapshot
Molecular mechanisms in podocytopathies: finding suitable targets for a new era of glomerular gene therapy
inferred← citeshttps://doi.org/10.1093/hmg/ddr141openalex-snapshot
Large-scale recombinant adeno-associated virus production
inferred← citeshttps://doi.org/10.1093/nar/gkz137openalex-snapshot
Antibody-targeted chromatin enables effective intracellular delivery and functionality of CRISPR/Cas9 expression plasmids
inferred← citeshttps://doi.org/10.1096/fj.202502611rropenalex-snapshot
Significant Enhancement of Adeno‐Associated Virus Vector Yield for Gene Therapy Using Multidimensional Optimization Strategies
inferred← citeshttps://doi.org/10.1097/iio.0000000000000362openalex-snapshot
Manufacturing of Viral Gene Therapies
inferred← citeshttps://doi.org/10.1097/sla.0000000000006436openalex-snapshot
Codon-Optimized and de novo–Synthesized E-Selectin/AAV2 Dose–Response Study for Vascular Regeneration Gene Therapy
inferred← citeshttps://doi.org/10.1101/2025.10.05.680573openalex-snapshot
High-Resolution Characterization of rAAV Genomes for Vector Quality Using Long-Read Sequencing
inferred← citeshttps://doi.org/10.1111/j.1442-9071.2009.02179.xopenalex-snapshot
Gene therapy for diseases of the cornea – a review
inferred← citeshttps://doi.org/10.1126/scitranslmed.3005795openalex-snapshot
Overcoming Preexisting Humoral Immunity to AAV Using Capsid Decoys
inferred← citeshttps://doi.org/10.1128/jvi.01769-19openalex-snapshot
Comparative Analysis of the Capsid Structures of AAVrh.10, AAVrh.39, and AAV8
inferred← citeshttps://doi.org/10.1134/s0006297923120179openalex-snapshot
Viral Vectors in Gene Replacement Therapy
inferred← citeshttps://doi.org/10.1166/jbn.2021.3183openalex-snapshot
Stability of Recombinant Mosaic Adeno-Associated Virus Vector rAAV/DJ/CAG at Different Temperature Conditions
inferred← citeshttps://doi.org/10.1177/01926233241298892openalex-snapshot
Systemic Toxicity of Recombinant Adeno-Associated Virus Gene Therapy Vectors
inferred← citeshttps://doi.org/10.1177/10430342261454324openalex-snapshot
AviNP-Seq: A Blindspot-Free Single-Molecule Framework for Unmasking AAV Genome Heterogeneity and Determining Packaging Limits
inferred← citeshttps://doi.org/10.1182/asheducation-2012.1.375openalex-snapshot
The gene therapy journey for hemophilia: are we there yet?
inferred← citeshttps://doi.org/10.1182/asheducation.v2012.1.375.3797885openalex-snapshot
The gene therapy journey for hemophilia: are we there yet?
inferred← citeshttps://doi.org/10.1182/blood-2012-05-423210openalex-snapshot
The gene therapy journey for hemophilia: are we there yet?
inferred← citeshttps://doi.org/10.1182/blood-2013-01-306647openalex-snapshot
Immune responses to AAV vectors: overcoming barriers to successful gene therapy
inferred← citeshttps://doi.org/10.1186/s12896-024-00853-6openalex-snapshot
Analysis of the impact of pluronic acid on the thermal stability and infectivity of AAV6.2FF
inferred← citeshttps://doi.org/10.1186/s12929-021-00760-4openalex-snapshot
Advances in the management of haemophilia: emerging treatments and their mechanisms
inferred← citeshttps://doi.org/10.1371/journal.pone.0013424openalex-snapshot
Gene Therapy in a Humanized Mouse Model of Familial Hypercholesterolemia Leads to Marked Regression of Atherosclerosis
inferred← citeshttps://doi.org/10.1371/journal.pone.0023101openalex-snapshot
Peptide Ligands Incorporated into the Threefold Spike Capsid Domain to Re-Direct Gene Transduction of AAV8 and AAV9 In Vivo
inferred← citeshttps://doi.org/10.1371/journal.pone.0061266openalex-snapshot
Intraganglionic AAV6 Results in Efficient and Long-Term Gene Transfer to Peripheral Sensory Nervous System in Adult Rats
inferred← citeshttps://doi.org/10.1371/journal.pone.0280242openalex-snapshot
Genome concentration, characterization, and integrity analysis of recombinant adeno-associated viral vectors using droplet digital PCR
inferred← citeshttps://doi.org/10.1517/14712598.2011.548799openalex-snapshot
AAV-mediated gene therapy for liver diseases: the prime candidate for clinical application?
inferred← citeshttps://doi.org/10.19080/ctbeb.2017.07.555704openalex-snapshot
Present Situation of Viral Vector Manufacturing and Ways to Overcome Potential Barriers in View of the Routine Large Scale Production and Use of Viral Vectors
inferred← citeshttps://doi.org/10.2147/tacg.s230720openalex-snapshot
Voretigene Neparvovec and Gene Therapy for Leber’s Congenital Amaurosis: Review of Evidence to Date
inferred← citeshttps://doi.org/10.2147/tacg.s31928openalex-snapshot
Developments in the treatment of hemophilia B: focus on emerging gene therapy
inferred← citeshttps://doi.org/10.2165/11595490-000000000-00000openalex-snapshot
Gene Therapy for Rheumatoid Arthritis
inferred← citeshttps://doi.org/10.2174/0118715273283786240408034408openalex-snapshot
CRISPR/Cas9 Gene Editing: A Novel Approach Towards Alzheimer's Disease Treatment
inferred← citeshttps://doi.org/10.2174/1389201016666150505122228openalex-snapshot
Scalable Downstream Strategies for Purification of Recombinant Adeno- Associated Virus Vectors in Light of the Properties
inferred← citeshttps://doi.org/10.2217/fvl-2017-0011openalex-snapshot
Understanding Capsid Assembly and Genome Packaging for Adeno-Associated Viruses
inferred← citeshttps://doi.org/10.30895/2221-996x-2022-22-1-6-22openalex-snapshot
Challenges in development and authorisation of gene therapy products
inferred← citeshttps://doi.org/10.3233/jnd-150113openalex-snapshot
Current Translational Research and Murine Models For Duchenne Muscular Dystrophy
inferred← citeshttps://doi.org/10.32469/10355/44658openalex-snapshot
Gene therapy in mouse models of spinal muscular atrophy :||using SMN gene replacement to address biological questions
inferred← citeshttps://doi.org/10.3342/kjorl-hns.2020.00836openalex-snapshot
Inner Ear Gene Therapy in Mouse Models of Genetic Hearing Loss
inferred← citeshttps://doi.org/10.3389/fbioe.2021.753480openalex-snapshot
Characterization of Recombinant Chimpanzee Adenovirus C68 Low and High-Density Particles: Impact on Determination of Viral Particle Titer
inferred← citeshttps://doi.org/10.3389/fceng.2022.830421openalex-snapshot
Process Improvement of Adeno-Associated Virus Production
inferred← citeshttps://doi.org/10.3389/fimmu.2020.00670openalex-snapshot
Human Immune Responses to Adeno-Associated Virus (AAV) Vectors
inferred← citeshttps://doi.org/10.3389/fimmu.2022.857276openalex-snapshot
Overcoming the Challenges Imposed by Humoral Immunity to AAV Vectors to Achieve Safe and Efficient Gene Transfer in Seropositive Patients
inferred← citeshttps://doi.org/10.3389/fnins.2021.803894openalex-snapshot
Application of CRISPR/Cas9 in Alzheimer’s Disease
inferred← citeshttps://doi.org/10.3389/fphy.2023.1076787openalex-snapshot
Stability and structural evolution of double-stranded DNA molecules under high pressures: A molecular dynamics study
inferred← citeshttps://doi.org/10.3390/biology15020136openalex-snapshot
Corneal Neovascularization: Pathogenesis, Current Insights and Future Strategies
inferred← citeshttps://doi.org/10.3390/cancers12061704openalex-snapshot
CRISPR-Mediated Non-Viral Site-Specific Gene Integration and Expression in T Cells: Protocol and Application for T-Cell Therapy
inferred← citeshttps://doi.org/10.3390/genes12040601openalex-snapshot
Accurate Quantification of AAV Vector Genomes by Quantitative PCR
inferred← citeshttps://doi.org/10.3390/pharmaceutics12080705openalex-snapshot
Development of New Strategies Using Extracellular Vesicles Loaded with Exogenous Nucleic Acid
inferred← citeshttps://doi.org/10.3390/pharmaceutics13020140openalex-snapshot
Strategies for Vaccination: Conventional Vaccine Approaches Versus New-Generation Strategies in Combination with Adjuvants
inferred← citeshttps://doi.org/10.3390/pharmaceutics18070814openalex-snapshot
Backbone-Minimised Nanoplasmid DNA Systems Enable High-Titre AAV Production in Suspension HEK293 Platforms
inferred← citeshttps://doi.org/10.38124/ijisrt20jul097openalex-snapshot
Degradation Study of Different Brands of Rosuvastatin Calcium Tablet in Bangladesh Using UV Spectrophotometer
inferred← citeshttps://doi.org/10.5282/edoc.10823openalex-snapshot
AAV2 vermittelte Transduktion von porcinem Myokard im Transplantationsmodell
inferred← citeshttps://doi.org/10.54097/hset.v36i.6282openalex-snapshot
Therapy for neurodegenerative Diseases and expectations
inferred← citeshttps://doi.org/10.5483/bmbrep.2021.54.1.245openalex-snapshot
Genome editing of immune cells using CRISPR/Cas9
inferred← citeshttps://doi.org/10.5603/hem.2015.0021openalex-snapshot
Postępy w leczeniu chorych na hemofilie
inferred← citeshttps://doi.org/10.56530/lcgc.na.st3379l8openalex-snapshot
Characterization of Adeno-Associated Virus (AAV) Gene Therapy Products
inferred← citeshttps://doi.org/10.5772/intechopen.100825openalex-snapshot
Recent Advances in Canine Medicine
inferred← citeshttps://doi.org/10.5772/intechopen.105085openalex-snapshot
Parvovirus Vectors: The Future of Gene Therapy
inferred← citeshttps://doi.org/10.6083/m4k935jkopenalex-snapshot
Novel strategies to improve viral gene targeting and therapeutic liver repopulation in vivo
inferred← citeshttps://doi.org/10.6084/m9.figshare.25698182openalex-snapshot
Additional file 1 of Analysis of the impact of pluronic acid on the thermal stability and infectivity of AAV6.2FF
inferred← citeshttps://doi.org/10.64898/2025.12.30.697113openalex-snapshot
Adeno-associated viruses (AAVs) induce dose-dependent neonatal ventriculomegaly following intracerebroventricular administration
inferred← citeshttps://doi.org/10.64898/2026.01.19.700387openalex-snapshot
Tailored Cell Cycle Modulation Enhances AAV Manufacturing: Balancing Arrest with Adaptive Stress Responses
inferred← citeshttps://doi.org/10.64898/2026.05.28.728583openalex-snapshot
Single Particle Adsorption and Response Quantification for Functional AAVx Titer and Dose Analysis
inferred← citeshttps://doi.org/10.70675/00cd6c50ze4b3z4b89z8f48z4d91a065dae0openalex-snapshot
Neurobiologie des atteintes centrales et saut d'exon thérapeutique dans un modèle murin de dystrophie musculaire de Duchenne
inferred← citeshttps://doi.org/10.70675/430aceacz50d2z426bz907dz876c55d1e935openalex-snapshot
Etude des réponses T CD8+ après transfert de gène par rAAV ciblant le muscle
inferred← citeshttps://doi.org/10.70675/6dbaff85za6adz4a23z9ab7zf8000ac559feopenalex-snapshot
Rémission de la polyarthrite rhumatoïde : apport des biomarqueurs et du mode d'administration des biothérapies
inferred← citeshttps://doi.org/10.70675/73a2ae45z8c46z41e6z8bd8z359a0cc98c9dopenalex-snapshot
Immunogenicity of recombinant Associated Virus-derived Vectors (rAAV) : how rAAV interact with the innate immune system ?
inferred← citeshttps://doi.org/10.70675/c5cff6daz8fe4z430cz80e6z97a11cc59c8eopenalex-snapshot
Characterization of rAAV vectors packaging in baculovirusinfected insect cells
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