On the public citation graph
Viral vector‐based gene therapies in the clinic
0 signed · 380 inferred · view as graph
Inferred edges come from two machine sources: sweeps of open repository metadata (mostly SSRN and Zenodo), and a bulk OpenAlex citation snapshot. Every row below is labelled with the one it came from. Neither is a complete citation index — absence here is not evidence of absence.
Is this your work? Sign in with ORCID and put your name on the
claims that are yours.
Reference health. See whether every reference in this work resolves to a
known work and none has been retracted — and get a dated CiteStamped
badge you can embed.
What this work says
Outgoing claims: the papers this work cites, builds on, or argues with.
inferredcites →https://doi.org/10.1001/jamaoncol.2019.6152openalex-snapshot
Objective Response Rate Among Patients With Locally Advanced or Metastatic Sarcoma Treated With Talimogene Laherparepvec in Combination With Pembrolizumab
inferredcites →https://doi.org/10.1002/biot.202000025openalex-snapshot
Production, Processing, and Characterization of Synthetic AAV Gene Therapy Vectors
inferredcites →https://doi.org/10.1002/btm2.10258openalex-snapshot
Viral vector‐based gene therapies in the clinic
inferredcites →https://doi.org/10.1002/jgm.619openalex-snapshot
Gene therapy clinical trials worldwide 1989–2004—an overview
inferredcites →https://doi.org/10.1007/978-3-030-03095-7_15openalex-snapshot
Large-Scale Clinical Manufacturing of AAV Vectors for Systemic Muscle Gene Therapy
inferredcites →https://doi.org/10.1007/s00262-017-1967-1openalex-snapshot
Combining talimogene laherparepvec with immunotherapies in melanoma and other solid tumors
inferredcites →https://doi.org/10.1007/s12185-018-2513-4openalex-snapshot
Advances in gene therapy for hemophilia: basis, current status, and future perspectives
inferredcites →https://doi.org/10.1007/s40259-017-0234-5openalex-snapshot
Adeno-Associated Virus (AAV) as a Vector for Gene Therapy
inferredcites →https://doi.org/10.1007/s40265-014-0339-9openalex-snapshot
Alipogene Tiparvovec: A Review of Its Use in Adults with Familial Lipoprotein Lipase Deficiency
inferredcites →https://doi.org/10.1016/b978-0-12-386509-0.00012-0openalex-snapshot
Adeno-Associated Virus Vectorology, Manufacturing, and Clinical Applications
inferredcites →https://doi.org/10.1016/j.biotechadv.2019.107502openalex-snapshot
The approved gene therapy drugs worldwide: from 1998 to 2019
inferredcites →https://doi.org/10.1016/j.coi.2021.03.008openalex-snapshot
Ebola virus disease: current vaccine solutions
inferredcites →https://doi.org/10.1016/j.coviro.2017.06.006openalex-snapshot
Origin of the retroviruses: when, where, and how?
inferredcites →https://doi.org/10.1016/j.neuron.2019.02.017openalex-snapshot
Therapeutic AAV Gene Transfer to the Nervous System: A Clinical Reality
inferredcites →https://doi.org/10.1016/j.neuron.2019.03.020openalex-snapshot
Therapeutic AAV Gene Transfer to the Nervous System: A Clinical Reality
inferredcites →https://doi.org/10.1016/j.omto.2018.12.005openalex-snapshot
A Phase I-II Study Using Rexin-G Tumor-Targeted Retrovector Encoding a Dominant-Negative Cyclin G1 Inhibitor for Advanced Pancreatic Cancer
inferredcites →https://doi.org/10.1016/j.vaccine.2013.03.020openalex-snapshot
Clinical development of Modified Vaccinia virus Ankara vaccines
inferredcites →https://doi.org/10.1016/j.ymthe.2004.07.013openalex-snapshot
Adenoviruses as vaccine vectors
inferredcites →https://doi.org/10.1016/j.ymthe.2006.05.009openalex-snapshot
Adeno-associated Virus Serotypes: Vector Toolkit for Human Gene Therapy
inferredcites →https://doi.org/10.1016/j.ymthe.2019.12.009openalex-snapshot
Retroviral Insertional Mutagenesis in Humans: Evidence for Four Genetic Mechanisms Promoting Expansion of Cell Clones
inferredcites →https://doi.org/10.1016/j.ymthe.2020.01.001openalex-snapshot
Immune Responses to Viral Gene Therapy Vectors
inferredcites →https://doi.org/10.1016/j.ymthe.2020.12.007openalex-snapshot
Current Clinical Applications of In Vivo Gene Therapy with AAVs
inferredcites →https://doi.org/10.1016/s0140-6736(20)32661-1openalex-snapshot
Safety and efficacy of the ChAdOx1 nCoV-19 vaccine (AZD1222) against SARS-CoV-2: an interim analysis of four randomised controlled trials in Brazil, South Africa, and the UK
inferredcites →https://doi.org/10.1016/s0958-1669(99)00007-5openalex-snapshot
Adenovirus vectors for gene delivery
inferredcites →https://doi.org/10.1016/s1525-0016(16)33110-0openalex-snapshot
301. AAV Capsid Engineering to Improve Transduction in Retina and Brain
inferredcites →https://doi.org/10.1021/acscentsci.1c00120openalex-snapshot
A Comprehensive Review of the Global Efforts on COVID-19 Vaccine Development
inferredcites →https://doi.org/10.1038/38410openalex-snapshot
Gene therapy - promises, problems and prospects
inferredcites →https://doi.org/10.1038/77283openalex-snapshot
Replicative adenoviruses for cancer therapy
inferredcites →https://doi.org/10.1038/83324openalex-snapshot
Viral vectors for gene therapy: the art of turning infectious agents into vehicles of therapeutics
inferredcites →https://doi.org/10.1038/d41573-020-00151-8openalex-snapshot
Evolution of the COVID-19 vaccine development landscape
inferredcites →https://doi.org/10.1038/d41573-021-00017-7openalex-snapshot
The clinical landscape for AAV gene therapies
inferredcites →https://doi.org/10.1038/gt.2008.170openalex-snapshot
Tailoring the AAV vector capsid for gene therapy
inferredcites →https://doi.org/10.1038/gt.2008.65openalex-snapshot
Manufacturing and characterizing AAV-based vectors for use in clinical studies
inferredcites →https://doi.org/10.1038/gt.2016.71openalex-snapshot
A brief account of viral vectors and their promise for gene therapy
inferredcites →https://doi.org/10.1038/mt.2008.76openalex-snapshot
Analysis of AAV Serotypes 1–9 Mediated Gene Expression and Tropism in Mice After Systemic Injection
inferredcites →https://doi.org/10.1038/mt.2009.126openalex-snapshot
Phase I/II and Phase II Studies of Targeted Gene Delivery In Vivo: Intravenous Rexin-G for Chemotherapy-resistant Sarcoma and Osteosarcoma
inferredcites →https://doi.org/10.1038/mt.2009.130openalex-snapshot
New Insights on Adenovirus as Vaccine Vectors
inferredcites →https://doi.org/10.1038/mt.2012.194openalex-snapshot
Endgame: Glybera Finally Recommended for Approval as the First Gene Therapy Drug in the European Union
inferredcites →https://doi.org/10.1038/mt.2016.10openalex-snapshot
Genome-editing Technologies for Gene and Cell Therapy
inferredcites →https://doi.org/10.1038/mtm.2016.34openalex-snapshot
Clinical development of gene therapy: results and lessons from recent successes
inferredcites →https://doi.org/10.1038/nbt1117-998openalex-snapshot
First AAV gene therapy poised for landmark approval
inferredcites →https://doi.org/10.1038/nrg2141openalex-snapshot
Engineering targeted viral vectors for gene therapy
inferredcites →https://doi.org/10.1038/nrg2988openalex-snapshot
Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges
inferredcites →https://doi.org/10.1038/nrg3742openalex-snapshot
Engineering adeno-associated viruses for clinical gene therapy
inferredcites →https://doi.org/10.1038/s41375-018-0106-0openalex-snapshot
Clinical use of lentiviral vectors
inferredcites →https://doi.org/10.1038/s41392-021-00487-6openalex-snapshot
Viral vector platforms within the gene therapy landscape
inferredcites →https://doi.org/10.1038/s41467-018-06076-6openalex-snapshot
Sub-2 Å Ewald curvature corrected structure of an AAV2 capsid variant
inferredcites →https://doi.org/10.1038/s41467-019-13786-yopenalex-snapshot
Structural basis for Fullerene geometry in a human endogenous retrovirus capsid
inferredcites →https://doi.org/10.1038/s41467-020-19505-2openalex-snapshot
The once and future gene therapy
inferredcites →https://doi.org/10.1038/s41573-019-0012-9openalex-snapshot
Adeno-associated virus vector as a platform for gene therapy delivery
inferredcites →https://doi.org/10.1038/s41576-019-0205-4openalex-snapshot
Engineering adeno-associated virus vectors for gene therapy
inferredcites →https://doi.org/10.1038/s41586-020-1978-5openalex-snapshot
The promise and challenge of therapeutic genome editing
inferredcites →https://doi.org/10.1038/s41591-020-0840-5openalex-snapshot
Safety and feasibility of CRISPR-edited T cells in patients with refractory non-small-cell lung cancer
inferredcites →https://doi.org/10.1038/s41598-017-08719-yopenalex-snapshot
Modified Vaccinia Virus Ankara Preferentially Targets Antigen Presenting Cells In Vitro, Ex Vivo and In Vivo
inferredcites →https://doi.org/10.1038/sj.gt.3302036openalex-snapshot
Molecular basis of the inflammatory response to adenovirus vectors
inferredcites →https://doi.org/10.1038/sj.gt.3302545openalex-snapshot
HSV trafficking and development of gene therapy vectors with applications in the nervous system
inferredcites →https://doi.org/10.1038/sj.onc.1209043openalex-snapshot
Retroviral insertional mutagenesis: past, present and future
inferredcites →https://doi.org/10.1056/nejmoa2101544openalex-snapshot
Safety and Efficacy of Single-Dose Ad26.COV2.S Vaccine against Covid-19
inferredcites →https://doi.org/10.1073/pnas.1001673107openalex-snapshot
A viral assembly factor promotes AAV2 capsid formation in the nucleolus
inferredcites →https://doi.org/10.1073/pnas.1423556112openalex-snapshot
Herpes simplex viral-vector design for efficient transduction of nonneuronal cells without cytotoxicity
inferredcites →https://doi.org/10.1080/14712598.2020.1757066openalex-snapshot
Engineering vaccinia virus as an immunotherapeutic battleship to overcome tumor heterogeneity
inferredcites →https://doi.org/10.1080/21645515.2017.1412896openalex-snapshot
Talimogene laherparepvec: First in class oncolytic virotherapy
inferredcites →https://doi.org/10.1080/21645515.2017.1419108openalex-snapshot
Development of novel vaccine vectors: Chimpanzee adenoviral vectors
inferredcites →https://doi.org/10.1089/10430340360535797openalex-snapshot
Optimization of the Generation and Propagation of Gutless Adenoviral Vectors
inferredcites →https://doi.org/10.1089/hum.2013.2527openalex-snapshot
Adenovirus: The First Effective In Vivo Gene Delivery Vector
inferredcites →https://doi.org/10.1089/hum.2017.218openalex-snapshot
The First Approved Gene Therapy Product for Cancer Ad- p53 (Gendicine): 12 Years in the Clinic
inferredcites →https://doi.org/10.1089/vim.2004.17.516openalex-snapshot
Vesicular Stomatitis Virus as an Oncolytic Vector
inferredcites →https://doi.org/10.1093/hmg/ddv451openalex-snapshot
Progress and challenges in viral vector manufacturing
inferredcites →https://doi.org/10.1099/jgv.0.000980openalex-snapshot
Recent advances in vesicular stomatitis virus-based oncolytic virotherapy: a 5-year update
inferredcites →https://doi.org/10.1111/cts.12466openalex-snapshot
Gene Therapy 2017: Progress and Future Directions
inferredcites →https://doi.org/10.1111/j.1749-6632.1994.tb21705.xopenalex-snapshot
Adenovirus‐Mediated in Vivo Gene Transfer
inferredcites →https://doi.org/10.1126/sciadv.1602670openalex-snapshot
Cryo-EM structure of human adenovirus D26 reveals the conservation of structural organization among human adenoviruses
inferredcites →https://doi.org/10.1126/science.272.5259.263openalex-snapshot
In Vivo Gene Delivery and Stable Transduction of Nondividing Cells by a Lentiviral Vector
inferredcites →https://doi.org/10.1126/science.aao7298openalex-snapshot
Structure of the herpes simplex virus 1 capsid with associated tegument protein complexes
inferredcites →https://doi.org/10.1128/jvi.72.2.926-933.1998openalex-snapshot
Production and Characterization of Improved Adenovirus Vectors with the E1, E2b, and E3 Genes Deleted
inferredcites →https://doi.org/10.1146/annurev-bioeng-071813-104938openalex-snapshot
Viral Vectors for Gene Therapy: Translational and Clinical Outlook
inferredcites →https://doi.org/10.1146/annurev-med-012017-043332openalex-snapshot
Entering the Modern Era of Gene Therapy
inferredcites →https://doi.org/10.1146/annurev-virology-092818-015530openalex-snapshot
Recombinant Adeno-Associated Virus Gene Therapy in Light of Luxturna (and Zolgensma and Glybera): Where Are We, and How Did We Get Here?
inferredcites →https://doi.org/10.1146/annurev-virology-101416-041936openalex-snapshot
Overcoming the Host Immune Response to Adeno-Associated Virus Gene Delivery Vectors: The Race Between Clearance, Tolerance, Neutralization, and Escape
inferredcites →https://doi.org/10.1161/01.atv.20.6.1452openalex-snapshot
Second-Generation Adenoviral Vectors Do Not Prevent Rapid Loss of Transgene Expression and Vector DNA From the Arterial Wall
inferredcites →https://doi.org/10.1182/blood-2018-07-820720openalex-snapshot
Update on clinical gene therapy for hemophilia
inferredcites →https://doi.org/10.1186/s11689-018-9234-0openalex-snapshot
Recent progress and considerations for AAV gene therapies targeting the central nervous system
inferredcites →https://doi.org/10.1186/s11689-018-9251-zopenalex-snapshot
Applying a network framework to the neurobiology of reading and dyslexia
inferredcites →https://doi.org/10.1371/journal.pone.0040385openalex-snapshot
A Novel Chimpanzee Adenovirus Vector with Low Human Seroprevalence: Improved Systems for Vector Derivation and Comparative Immunogenicity
inferredcites →https://doi.org/10.14440/jbm.2016.102openalex-snapshot
Inexpensive, serotype-independent protocol for native and bioengineered recombinant adeno-associated virus purification
inferredcites →https://doi.org/10.1517/14712598.2010.481666openalex-snapshot
Rexin-G, a targeted genetic medicine for cancer
inferredcites →https://doi.org/10.1517/14712598.2015.993374openalex-snapshot
Adenoviruses as gene/vaccine delivery vectors: promises and pitfalls
inferredcites →https://doi.org/10.18609/cgti.2018.083openalex-snapshot
Overcoming Bottlenecks in AAV Manufacturing for Gene Therapy
inferredcites →https://doi.org/10.18632/oncotarget.231openalex-snapshot
The Challenge for Gene Therapy: Innate Immune Response to Adenoviruses
inferredcites →https://doi.org/10.2174/138920112800958814openalex-snapshot
Oncolytic HSV-1 Virotherapy: Clinical Experience and Opportunities for Progress
inferredcites →https://doi.org/10.2174/1566523052997514openalex-snapshot
Retroviral Gene Therapy: Safety Issues and Possible Solutions
inferredcites →https://doi.org/10.2174/156652311795684740openalex-snapshot
Current Advances in Retroviral Gene Therapy
inferredcites →https://doi.org/10.2174/156652312802762518openalex-snapshot
Development of Sendai Virus Vectors and their Potential Applications in Gene Therapy and Regenerative Medicine
inferredcites →https://doi.org/10.2174/1566523213666131125095046openalex-snapshot
Adenovirus Vectors for Gene Therapy, Vaccination and Cancer Gene Therapy
inferredcites →https://doi.org/10.2174/1568009617666170222125035openalex-snapshot
Clinical Trials with Oncolytic Measles Virus: Current Status and Future Prospects
inferredcites →https://doi.org/10.2174/1568009618666171129221503openalex-snapshot
Oncorine, the World First Oncolytic Virus Medicine and its Update in China
inferredcites →https://doi.org/10.2174/1874357901004010123openalex-snapshot
HSV Recombinant Vectors for Gene Therapy
inferredcites →https://doi.org/10.2174/1874357901004030123openalex-snapshot
HSV Recombinant Vectors for Gene Therapy~!2009-12-17~!2010-13-31~!2010-06-17~!
inferredcites →https://doi.org/10.2217/imt-2019-0033openalex-snapshot
Talimogene Laherparepvec: Review of its Mechanism of Action and Clinical Efficacy and Safety
inferredcites →https://doi.org/10.32388/mrapt2openalex-snapshot
National Human Genome Research Institute
inferredcites →https://doi.org/10.3389/fgene.2019.00868openalex-snapshot
Development and Clinical Translation of Approved Gene Therapy Products for Genetic Disorders
inferredcites →https://doi.org/10.3389/fonc.2019.00297openalex-snapshot
Gene Therapy Leaves a Vicious Cycle
inferredcites →https://doi.org/10.3390/v10060316openalex-snapshot
Non-Primate Lentiviral Vectors and Their Applications in Gene Therapy for Ocular Disorders
inferredcites →https://doi.org/10.3390/v11020102openalex-snapshot
Adeno-Associated Virus (AAV) Versus Immune Response
inferredcites →https://doi.org/10.3390/v3060677openalex-snapshot
Gammaretroviral Vectors: Biology, Technology and Application
inferredcites →https://doi.org/10.3390/vaccines9030190openalex-snapshot
Development of Pandemic Vaccines: ERVEBO Case Study
What points at this work
Incoming claims: where this work appears in other papers’ reference lists and arguments.
inferred← citeshttps://doi.org/10.2139/ssrn.4592842openalex-extracted
Separation of Full and Empty AAV Capsids by Anion-Exchange Chromatography Using Choline-Type Salts
inferred← citeshttps://doi.org/10.2139/ssrn.4658165openalex-extracted
Adeno-Associated Virus Analysis by Size Exclusion Chromatography within 3 Minutes Using Short Bio-Inert Columns Made with 3 Μm Particles Operated at High Flowrates
inferred← citeshttps://doi.org/10.1002/9781394236145.ch17openalex-snapshot
Receptomics and Extracellular Interactomics for Biotherapeutic Characterization
inferred← citeshttps://doi.org/10.1002/9781394271566.ch1openalex-snapshot
Introduction to Viral Vectors
inferred← citeshttps://doi.org/10.1002/9781394271566.ch7openalex-snapshot
DNA‐ and RNA‐Based Viral Vectors
inferred← citeshttps://doi.org/10.1002/adfm.202312038openalex-snapshot
Oxidized mRNA Lipid Nanoparticles for In Situ Chimeric Antigen Receptor Monocyte Engineering
inferred← citeshttps://doi.org/10.1002/adma.202404608openalex-snapshot
Beyond Lipids: Exploring Advances in Polymeric Gene Delivery in the Lipid Nanoparticles Era
inferred← citeshttps://doi.org/10.1002/advs.202201293openalex-snapshot
Red Blood Cell Anchoring Enables Targeted Transduction and Re‐Administration of AAV‐Mediated Gene Therapy
inferred← citeshttps://doi.org/10.1002/advs.202302253openalex-snapshot
Bioorthogonal CRISPR/Cas9‐Drug Conjugate: A Combinatorial Nanomedicine Platform
inferred← citeshttps://doi.org/10.1002/advs.202309917openalex-snapshot
Design of PD‐L1‐Targeted Lipid Nanoparticles to Turn on PTEN for Efficient Cancer Therapy
inferred← citeshttps://doi.org/10.1002/alz.70578openalex-snapshot
Twenty years of therapeutic development in tauopathy mouse models: a scoping review
inferred← citeshttps://doi.org/10.1002/bies.202300037openalex-snapshot
Suicide gene‐enabled cell therapy: A novel approach to scalable human pluripotent stem cell quality control
inferred← citeshttps://doi.org/10.1002/biot.202200513openalex-snapshot
Comprehensive mRNA‐sequencing‐based characterization of three HEK‐293 cell lines during an rAAV production process for gene therapy applications
inferred← citeshttps://doi.org/10.1002/biot.202400526openalex-snapshot
Towards a Platform Chromatography Purification Process for Adeno‐Associated Virus (AAV)
inferred← citeshttps://doi.org/10.1002/bit.28980openalex-snapshot
Development of an HEK293 Suspension Cell Culture Medium, Transient Transfection Optimization Workflow, and Analytics for Batch rAAV Manufacturing
inferred← citeshttps://doi.org/10.1002/bit.70289openalex-snapshot
Nanocarrier‐Based Gene Delivery Systems: Mechanisms, Clinical Translation, and Future Perspectives
inferred← citeshttps://doi.org/10.1002/btm2.10483openalex-snapshot
Biomimetic nanotherapeutics for targeted drug delivery to glioblastoma multiforme
inferred← citeshttps://doi.org/10.1002/btm2.70070openalex-snapshot
Low‐cost, handheld, multi‐pulse electroporators for simplified nucleic acid delivery in skin
inferred← citeshttps://doi.org/10.1002/btm2.70106openalex-snapshot
Viral vector‐based gene therapies in the clinic: An update
inferred← citeshttps://doi.org/10.1002/cnr2.70425openalex-snapshot
Toward Precision Medicine: Gene Therapy Applications in the Management of Uveal Melanoma
inferred← citeshttps://doi.org/10.1002/exp.20230165openalex-snapshot
Exploring precision treatments in immune‐mediated inflammatory diseases: Harnessing the infinite potential of nucleic acid delivery
inferred← citeshttps://doi.org/10.1002/jcph.2141openalex-snapshot
Clinical Pharmacology Considerations on Recombinant Adeno‐Associated Virus–Based Gene Therapy
inferred← citeshttps://doi.org/10.1002/jgm.3721openalex-snapshot
Gene therapy clinical trials worldwide to 2023—an update
inferred← citeshttps://doi.org/10.1002/mco2.70964openalex-snapshot
High‐Content CRISPR Screening: Methods and Applications
inferred← citeshttps://doi.org/10.1002/mog2.55openalex-snapshot
Viral vector‐based cancer treatment and current clinical applications
inferred← citeshttps://doi.org/10.1007/978-3-031-11570-7_2openalex-snapshot
Genetic Engineering of the Kidney
inferred← citeshttps://doi.org/10.1007/978-3-031-28489-2_11openalex-snapshot
Quantification of Virus Infectivity: The Key Assay for the Development of Viral Therapeutics
inferred← citeshttps://doi.org/10.1007/978-3-031-47567-2_5openalex-snapshot
Pulmonary Delivery of Nucleic Acids
inferred← citeshttps://doi.org/10.1007/978-3-031-55653-1_5openalex-snapshot
Drug Delivery Systems for Tendon and Ligament
inferred← citeshttps://doi.org/10.1007/978-3-031-80185-3_2openalex-snapshot
Nanoparticle-Mediated Gene Therapy for Neurological Disorders
inferred← citeshttps://doi.org/10.1007/978-3-031-81787-8_5openalex-snapshot
Hope Unlocked: Gene Therapy with Viral Vectors and Gene Editing
inferred← citeshttps://doi.org/10.1007/978-3-031-93425-4_6openalex-snapshot
Genetically Mediated Cell Membrane Engineering Strategies and Their Scope in Biomedical Applications
inferred← citeshttps://doi.org/10.1007/978-981-97-4974-4_9openalex-snapshot
Gene Therapy and Gene Editing
inferred← citeshttps://doi.org/10.1007/s00109-023-02397-2openalex-snapshot
A gene therapy targeting medium-chain acyl-CoA dehydrogenase (MCAD) did not protect against diabetes-induced cardiac pathology
inferred← citeshttps://doi.org/10.1007/s11095-022-03328-5openalex-snapshot
Red Blood Cell Inspired Strategies for Drug Delivery: Emerging Concepts and New Advances
inferred← citeshttps://doi.org/10.1007/s11706-023-0637-9openalex-snapshot
Dopamine-mimetic-coated polyamidoamine-functionalized Fe3O4 nanoparticles for safe and efficient gene delivery
inferred← citeshttps://doi.org/10.1007/s12033-023-00821-zopenalex-snapshot
Coding Therapeutic Nucleic Acids from Recombinant Proteins to Next-Generation Vaccines: Current Uses, Limitations, and Future Horizons
inferred← citeshttps://doi.org/10.1007/s12033-024-01301-8openalex-snapshot
Nanotechnology and CRISPR/Cas-Mediated Gene Therapy Strategies: Potential Role for Treating Genetic Disorders
inferred← citeshttps://doi.org/10.1007/s12195-026-00886-1openalex-snapshot
Barrier Function of the Extracellular Matrix in AAV Gene Therapy
inferred← citeshttps://doi.org/10.1007/s12257-025-00216-8openalex-snapshot
Lentiviral Surface Engineering via Tris(2-Carboxyethyl)Phosphine-mediated HEK-293T Cell Modification
inferred← citeshttps://doi.org/10.1007/s12672-025-03070-5openalex-snapshot
mRNA vaccines and SiRNAs targeting cancer immunotherapy: challenges and opportunities
inferred← citeshttps://doi.org/10.1007/s13205-025-04366-7openalex-snapshot
Advances in viral vector-based delivery systems for gene therapy: a comprehensive review
inferred← citeshttps://doi.org/10.1007/s13346-023-01362-3openalex-snapshot
Technological advances in the use of viral and non-viral vectors for delivering genetic and non-genetic cargos for cancer therapy
inferred← citeshttps://doi.org/10.1016/b978-0-323-90120-8.00003-4openalex-snapshot
Disease-specific interventions: The use of cell and gene therapies for Parkinson disease
inferred← citeshttps://doi.org/10.1016/b978-0-443-13344-2.00003-1openalex-snapshot
Preclinical development of viral vector gene therapies
inferred← citeshttps://doi.org/10.1016/b978-0-443-13474-6.00002-0openalex-snapshot
Future prospects and challenges to central nervous system drug delivery; A shortcoming towards treatment of neurodegenerative disease
inferred← citeshttps://doi.org/10.1016/bs.acr.2023.03.005openalex-snapshot
Applications of tissue-specific and cancer-selective gene promoters for cancer diagnosis and therapy
inferred← citeshttps://doi.org/10.1016/bs.apcsb.2023.11.013openalex-snapshot
Technological advancements in viral vector designing and optimization for therapeutic applications
inferred← citeshttps://doi.org/10.1016/j.ab.2023.115421openalex-snapshot
Separation of full and empty adeno-associated virus capsids by anion-exchange chromatography using choline-type salts
inferred← citeshttps://doi.org/10.1016/j.actbio.2025.12.047openalex-snapshot
Rapidly dissolving biomaterials for high-efficiency viral transduction
inferred← citeshttps://doi.org/10.1016/j.actbio.2026.06.027openalex-snapshot
Peptide–amphiphile complex coacervates for high-capacity genetic material delivery under physiological conditions
inferred← citeshttps://doi.org/10.1016/j.addr.2023.114962openalex-snapshot
Evolution of nanomedicine formulations for targeted delivery and controlled release
inferred← citeshttps://doi.org/10.1016/j.addr.2025.115639openalex-snapshot
Aptamer-based applications in delivering cancer gene therapies and beyond: state of the art and the missing links to clinical translation
inferred← citeshttps://doi.org/10.1016/j.addr.2026.115958openalex-snapshot
From conventional biologics–device combination products to advanced therapies: current state and future trends in patient-centric delivery
inferred← citeshttps://doi.org/10.1016/j.ajps.2025.101041openalex-snapshot
Functionalized chitosan as nano-delivery platform for CRISPR-Cas9 in cancer treatment
inferred← citeshttps://doi.org/10.1016/j.apsb.2026.09.027openalex-snapshot
CRISPR/Cas based genome editing for liver diseases: Promise and challenge
inferred← citeshttps://doi.org/10.1016/j.bbrep.2024.101771openalex-snapshot
CRISPR/Cas9 technology in the modeling of and treatment of mucopolysaccharidosis
inferred← citeshttps://doi.org/10.1016/j.bbrep.2025.102010openalex-snapshot
The effect of enhancers on the lentiviral transduction efficiency in the human RPE cells: Insights for advancing retinal gene therapies
inferred← citeshttps://doi.org/10.1016/j.bej.2023.108814openalex-snapshot
Process for production of chimeric antigen receptor-transducing lentivirus particles using infection with replicon particles containing self-replicating RNAs
inferred← citeshttps://doi.org/10.1016/j.bioelechem.2021.107994openalex-snapshot
Revisiting the role of pulsed electric fields in overcoming the barriers to in vivo gene electrotransfer
inferred← citeshttps://doi.org/10.1016/j.biomaterials.2023.122464openalex-snapshot
Protein-based nanoparticles for therapeutic nucleic acid delivery
inferred← citeshttps://doi.org/10.1016/j.biotechadv.2024.108391openalex-snapshot
Advances and opportunities in process analytical technologies for viral vector manufacturing
inferred← citeshttps://doi.org/10.1016/j.carres.2024.109326openalex-snapshot
Tricine-modified chitosan as a strategy for enhancing hydrophilicity and gene delivery
inferred← citeshttps://doi.org/10.1016/j.cbi.2024.111000openalex-snapshot
Cationic cycloamylose based nucleic acid nanocarriers
inferred← citeshttps://doi.org/10.1016/j.cej.2022.140962openalex-snapshot
Direct cytosolic delivery of DNA by creating fast closable holes in the cell membrane
inferred← citeshttps://doi.org/10.1016/j.celrep.2023.112903openalex-snapshot
AAV5-mediated manipulation of insulin expression in choroid plexus has long-term metabolic and behavioral consequences
inferred← citeshttps://doi.org/10.1016/j.chroma.2023.464337openalex-snapshot
The downstream bioprocess toolbox for therapeutic viral vectors
inferred← citeshttps://doi.org/10.1016/j.chroma.2024.464684openalex-snapshot
Adeno-associated virus analysis by size exclusion chromatography within 3 minutes using short bio-inert columns made with 3 µm particles operated at high flowrates
inferred← citeshttps://doi.org/10.1016/j.cis.2023.102989openalex-snapshot
Cold atmospheric plasma mediated cell membrane permeation and gene delivery-empirical interventions and pertinence
inferred← citeshttps://doi.org/10.1016/j.cmi.2022.05.015openalex-snapshot
Infectious diseases and inborn errors of immunity
inferred← citeshttps://doi.org/10.1016/j.coi.2025.102611openalex-snapshot
HLA-B27 as a potential target for the cure of axial spondyloarthritis
inferred← citeshttps://doi.org/10.1016/j.cont.2024.101311openalex-snapshot
Unlocking potential: Herpes Simplex Virus Type 1-based gene therapy in functional urology
inferred← citeshttps://doi.org/10.1016/j.copbio.2022.102828openalex-snapshot
Upstream continuous processing: recent advances in production of biopharmaceuticals and challenges in manufacturing
inferred← citeshttps://doi.org/10.1016/j.critrevonc.2026.105303openalex-snapshot
Targeted cancer therapy: A comprehensive review of strategies in drug development
inferred← citeshttps://doi.org/10.1016/j.ejbt.2024.07.005openalex-snapshot
The significance of chemical transfection/transduction enhancers in promoting the viral vectors-assisted gene delivery approaches: A focus on potentials for inherited retinal diseases
inferred← citeshttps://doi.org/10.1016/j.ejps.2024.106898openalex-snapshot
Comparison of ionizable lipids for lipid nanoparticle mediated DNA delivery
inferred← citeshttps://doi.org/10.1016/j.ijpharm.2024.123864openalex-snapshot
Nanogels: Smart tools to enlarge the therapeutic window of gene therapy
inferred← citeshttps://doi.org/10.1016/j.ijpharm.2025.125910openalex-snapshot
Complementary approaches and advanced technologies in ameliorating rate of wound healing
inferred← citeshttps://doi.org/10.1016/j.ijpharm.2026.126641openalex-snapshot
In vitro evaluation of a cationic polymer-lipid conjugate as a potential nanosystem for gene delivery
inferred← citeshttps://doi.org/10.1016/j.ijpx.2024.100283openalex-snapshot
Comprehensive analysis of lipid nanoparticle formulation and preparation for RNA delivery
inferred← citeshttps://doi.org/10.1016/j.jbiotec.2026.03.018openalex-snapshot
Enhancing the utility of Sendai virus–based vectors through antiviral compound–mediated removal
inferred← citeshttps://doi.org/10.1016/j.jconrel.2022.10.061openalex-snapshot
Mechanisms and challenges of nanocarriers as non-viral vectors of therapeutic genes for enhanced pulmonary delivery
inferred← citeshttps://doi.org/10.1016/j.jconrel.2024.01.026openalex-snapshot
Enhanced gene transfection and induction of apoptosis in melanoma cells by branched poly(β-amino ester)s with uniformly distributed branching units
inferred← citeshttps://doi.org/10.1016/j.jconrel.2025.02.060openalex-snapshot
Injectable polyplex-loaded glycol chitosan thermogel for efficient and safe inner ear gene delivery
inferred← citeshttps://doi.org/10.1016/j.jconrel.2025.114337openalex-snapshot
Elastin-like peptides for efficient and safe delivery of mRNA
inferred← citeshttps://doi.org/10.1016/j.jconrel.2026.114841openalex-snapshot
Retinal gene therapies for inherited ocular diseases: Translational delivery strategies from bench to bedside
inferred← citeshttps://doi.org/10.1016/j.jconrel.2026.115082openalex-snapshot
Delivering living medicines with polysaccharide derivatives for disease treatment
inferred← citeshttps://doi.org/10.1016/j.jddst.2022.103964openalex-snapshot
Challenges to perform an efficiently gene therapy adopting non-viral vectors: Melanoma landscape
inferred← citeshttps://doi.org/10.1016/j.jddst.2024.106413openalex-snapshot
Unlocking therapeutic potential of siRNA-based drug delivery system for treatment of Alzheimer's disease
inferred← citeshttps://doi.org/10.1016/j.jmb.2025.169473openalex-snapshot
Retroviral Vector Technology for Gene Therapy: History, Current Landscape, and Future Prospects
inferred← citeshttps://doi.org/10.1016/j.jphotochem.2024.115730openalex-snapshot
GFP chromophore derived amphiphiles containing [12]aneN3 and biotin moieties as bio-imaging and targeting nonviral gene vectors
inferred← citeshttps://doi.org/10.1016/j.jviromet.2023.114688openalex-snapshot
Local and systemic administration of AAV vectors with alphaherpesvirus latency-associated promoter 2 drives potent transgene expression in mouse liver, kidney, and skeletal muscle
inferred← citeshttps://doi.org/10.1016/j.lssr.2022.08.006openalex-snapshot
Harnessing nucleic acid technologies for human health on earth and in space
inferred← citeshttps://doi.org/10.1016/j.memsci.2024.123276openalex-snapshot
Development of a local wall concentration model for the design of single pass tangential flow filtration (SPTFF) systems with viral vector surrogates
inferred← citeshttps://doi.org/10.1016/j.mtbio.2022.100525openalex-snapshot
Nanosystems for gene therapy targeting brain damage caused by viral infections
inferred← citeshttps://doi.org/10.1016/j.neuron.2025.03.031openalex-snapshot
Specific targeting of brain endothelial cells using enhancer AAV vectors
inferred← citeshttps://doi.org/10.1016/j.neurot.2024.e00434openalex-snapshot
Neurosurgical gene therapy for central nervous system diseases
inferred← citeshttps://doi.org/10.1016/j.omta.2026.201700openalex-snapshot
Manufacture of adeno-associated virus vectors by a novel human-derived cell line HAT and comprehensive evaluation of the vectors
inferred← citeshttps://doi.org/10.1016/j.omta.2026.201739openalex-snapshot
Efficient and safe lung gene delivery using AAV6.2FF in neonatal pigs demonstrates pediatric translational potential
inferred← citeshttps://doi.org/10.1016/j.omtm.2023.101153openalex-snapshot
Iron oxide-coupled CRISPR-nCas9-based genome editing assessment in mucopolysaccharidosis IVA mice
inferred← citeshttps://doi.org/10.1016/j.omtm.2024.101241openalex-snapshot
Combining CRISPR-Cas-mediated terminal resolution with a novel genetic workflow to achieve high-diversity adenoviral libraries
inferred← citeshttps://doi.org/10.1016/j.omtm.2024.101370openalex-snapshot
Characterization of the function of Adenovirus L4 gene products and their impact on AAV vector production
inferred← citeshttps://doi.org/10.1016/j.omtm.2024.101377openalex-snapshot
Structural characterization and epitope mapping of the AAVX affinity purification ligand
inferred← citeshttps://doi.org/10.1016/j.omtm.2025.101582openalex-snapshot
Genome-replicating HC-AdV: A novel high-capacity adenoviral vector class featuring enhanced in situ payload expression
inferred← citeshttps://doi.org/10.1016/j.omtm.2025.101597openalex-snapshot
A novel gene delivery platform based on a commensal human anellovirus demonstrates transduction in multiple tissue types
inferred← citeshttps://doi.org/10.1016/j.omtm.2025.101629openalex-snapshot
The amazing AAV capsids: Into the structure-verse
inferred← citeshttps://doi.org/10.1016/j.omtn.2023.08.020openalex-snapshot
Novel hybrid silicon-lipid nanoparticles deliver a siRNA to cure autosomal dominant osteopetrosis in mice. Implications for gene therapy in humans
inferred← citeshttps://doi.org/10.1016/j.omtn.2024.102426openalex-snapshot
Flow rate modulates focused ultrasound-mediated vascular delivery of microRNA
inferred← citeshttps://doi.org/10.1016/j.omtn.2025.102582openalex-snapshot
Mass photometry as a robust method for characterizing adeno-associated virus critical quality attributes in gene therapy vector
inferred← citeshttps://doi.org/10.1016/j.omtn.2025.102739openalex-snapshot
A novel gene therapy platform for the treatment of type 2 diabetes and obesity
inferred← citeshttps://doi.org/10.1016/j.omtn.2026.103084openalex-snapshot
Cas12a chRDNA-mediated in vivo genome editing for high specificity functional gene disruption
inferred← citeshttps://doi.org/10.1016/j.omton.2024.200867openalex-snapshot
ADEVO: Proof-of-concept of adenovirus-directed EVOlution by random peptide display on the fiber knob
inferred← citeshttps://doi.org/10.1016/j.onano.2024.100215openalex-snapshot
Fundamentals behind the success of nanotechnology in cancer treatment and diagnosis
inferred← citeshttps://doi.org/10.1016/j.pharmr.2025.100065openalex-snapshot
Pharmaceutical perspectives on oligonucleotide therapeutics and delivery systems
inferred← citeshttps://doi.org/10.1016/j.reth.2024.12.007openalex-snapshot
Viral-based gene therapy clinical trials for immune deficiencies and blood disorders from 2013 until 2023 - an overview
inferred← citeshttps://doi.org/10.1016/j.sdentj.2024.03.015openalex-snapshot
Application of BMP-2 and its gene delivery vehicles in dentistry
inferred← citeshttps://doi.org/10.1016/j.seppur.2025.133051openalex-snapshot
Downstream processing of AAV based gene therapy vectors
inferred← citeshttps://doi.org/10.1016/j.socscimed.2025.118687openalex-snapshot
Public sector innovation and the constraints of ‘platform thinking’: An account of Johnson & Johnson's adenoviral vector vaccines
inferred← citeshttps://doi.org/10.1016/j.tig.2022.12.001openalex-snapshot
Clinical progress in genome-editing technology and in vivo delivery techniques
inferred← citeshttps://doi.org/10.1016/j.trac.2023.117088openalex-snapshot
Chromatographic strategies for the analytical characterization of adeno-associated virus vector-based gene therapy products
inferred← citeshttps://doi.org/10.1016/j.ultsonch.2024.107173openalex-snapshot
Hydrogel carrier with bubble vibration enhancer for ultrasound-triggered drug release
inferred← citeshttps://doi.org/10.1016/j.xcrm.2026.102639openalex-snapshot
Therapeutic base editing alleviates restrictive cardiomyopathy
inferred← citeshttps://doi.org/10.1016/j.xphs.2022.12.012openalex-snapshot
Measurement of Adenovirus-Based Vector Heterogeneity
inferred← citeshttps://doi.org/10.1016/j.ymthe.2023.02.015openalex-snapshot
A high-fidelity RNA-targeting Cas13 restores paternal Ube3a expression and improves motor functions in Angelman syndrome mice
inferred← citeshttps://doi.org/10.1016/j.ymthe.2023.03.024openalex-snapshot
CRISPR-Cas-mediated transcriptional modulation: The therapeutic promises of CRISPRa and CRISPRi
inferred← citeshttps://doi.org/10.1016/j.ymthe.2023.09.012openalex-snapshot
Optimal delivery of RNA interference by viral vectors for cancer therapy
inferred← citeshttps://doi.org/10.1016/j.ymthe.2024.01.033openalex-snapshot
Tau reduction with artificial microRNAs modulates neuronal physiology and improves tauopathy phenotypes in mice
inferred← citeshttps://doi.org/10.1016/j.ymthe.2025.09.041openalex-snapshot
Designing nucleic acid-based therapeutics for cancer treatment: Updates on the state of the art
inferred← citeshttps://doi.org/10.1016/j.ymthe.2026.07.045openalex-snapshot
Triple-AAV intein-mediated gene therapy ameliorates dystrophic phenotype in MDC1A mice
inferred← citeshttps://doi.org/10.1016/s1637-5017(23)91112-9openalex-snapshot
10.1016/s1637-5017(23)91112-9
inferred← citeshttps://doi.org/10.1021/acs.chemrev.3c00062openalex-snapshot
Tumor Abnormality-Oriented Nanomedicine Design
inferred← citeshttps://doi.org/10.1021/acs.chemrev.4c00142openalex-snapshot
Mechanisms and Delivery of tRNA Therapeutics
inferred← citeshttps://doi.org/10.1021/acs.langmuir.5c05024openalex-snapshot
Enhancing Deoxyribonucleic Acid Delivery Efficiency via pH-Responsive Metal-Tannic Acid Cross-Linking Encapsulation
inferred← citeshttps://doi.org/10.1021/acsabm.3c00725openalex-snapshot
Bioinspired and Biomimetic Gene Delivery Systems
inferred← citeshttps://doi.org/10.1021/acsabm.3c00886openalex-snapshot
Nucleic Acid Delivery Nanotechnologies for In Vivo Cell Programming
inferred← citeshttps://doi.org/10.1021/acsabm.5c00742openalex-snapshot
Photothermal Micro-Nano Solid Substrates for Intracellular Delivery via Laser-Assisted Photoporation
inferred← citeshttps://doi.org/10.1021/acsami.5c15987openalex-snapshot
Exosome-Mediated RUNX3 DNA Delivery for Lung Cancer Therapy
inferred← citeshttps://doi.org/10.1021/acsanm.2c04279openalex-snapshot
Peptide-DNA Co-Assembled Nanoparticles as a Nonviral Vector for Gene Delivery with High Transgene Expression
inferred← citeshttps://doi.org/10.1021/acsapm.5c03696openalex-snapshot
Spherical Polyelectrolyte Brushes for Nonviral Efficient Gene Delivery
inferred← citeshttps://doi.org/10.1021/acsbiomaterials.4c01595openalex-snapshot
Enhancing Gene Delivery to Breast Cancer with Highly Efficient siRNA Loading and pH-Responsive Small Extracellular Vesicles
inferred← citeshttps://doi.org/10.1021/acschembio.6c00383openalex-snapshot
Intracellular Delivery of Peptides and Proteins with an Engineered Membrane Translocation Domain
inferred← citeshttps://doi.org/10.1021/acsnano.5c16533openalex-snapshot
Mechanisms of Adeno-Associated Virus Serotype 9 Vector Characterization and Quality Control through Solid-State Nanopores
inferred← citeshttps://doi.org/10.1038/s41392-026-02793-3openalex-snapshot
Engineered tRNA reduces vision loss in a mouse model of Leber congenital amaurosis
inferred← citeshttps://doi.org/10.1038/s41417-025-00926-4openalex-snapshot
AAV for ovarian cancer gene therapy
inferred← citeshttps://doi.org/10.1038/s41571-024-00883-1openalex-snapshot
Nucleic acid-based drugs for patients with solid tumours
inferred← citeshttps://doi.org/10.1038/s41578-024-00766-yopenalex-snapshot
Delivering living medicines with biomaterials
inferred← citeshttps://doi.org/10.1038/s41583-023-00776-9openalex-snapshot
Cell type-specific roles of APOE4 in Alzheimer disease
inferred← citeshttps://doi.org/10.1038/s41583-024-00829-7openalex-snapshot
Gene therapy for CNS disorders: modalities, delivery and translational challenges
inferred← citeshttps://doi.org/10.1038/s41587-024-02437-3openalex-snapshot
Lung and liver editing by lipid nanoparticle delivery of a stable CRISPR–Cas9 ribonucleoprotein
inferred← citeshttps://doi.org/10.1038/s41587-024-02528-1openalex-snapshot
Nanocarrier imaging at single-cell resolution across entire mouse bodies with deep learning
inferred← citeshttps://doi.org/10.1038/s41587-025-02664-2openalex-snapshot
Self-assembling protein nanoparticles for cytosolic delivery of nucleic acids and proteins
inferred← citeshttps://doi.org/10.1038/s41598-022-21867-0openalex-snapshot
An efficient rAAV vector for protein expression in cortical parvalbumin expressing interneurons
inferred← citeshttps://doi.org/10.1038/s42256-023-00787-2openalex-snapshot
Variational autoencoder for design of synthetic viral vector serotypes
inferred← citeshttps://doi.org/10.1038/s44222-024-00255-5openalex-snapshot
The physico-chemical landscape of extracellular vesicles
inferred← citeshttps://doi.org/10.1038/s44318-025-00389-1openalex-snapshot
Parasitic plasmids are anchored to inactive regions of eukaryotic chromosomes through a nucleosome signal
inferred← citeshttps://doi.org/10.1039/9781837675555-00041openalex-snapshot
Recent Advances and Challenges in Targeted Drug Delivery Using Biofunctional Coatings
inferred← citeshttps://doi.org/10.1039/d2cc02759copenalex-snapshot
Tumor microenvironment responsive nanocarriers for gene therapy
inferred← citeshttps://doi.org/10.1039/d5lc01050kopenalex-snapshot
High-recovery AAV clarification using a multiplexed spiral inertial microfluidic platform
inferred← citeshttps://doi.org/10.1039/d5na00169bopenalex-snapshot
Synthesis, characterization, and evaluation of low molecular weight poly(β-amino ester) nanocarriers for enhanced T cell transfection and gene delivery in cancer immunotherapy
inferred← citeshttps://doi.org/10.1063/5.0197742openalex-snapshot
Advanced coacervation-driven nanoscale polymeric assemblies for biomedical applications
inferred← citeshttps://doi.org/10.1073/pnas.2218247120openalex-snapshot
Biolistic delivery of liposomes protected in metal-organic frameworks
inferred← citeshttps://doi.org/10.1080/00914037.2025.2475878openalex-snapshot
In vitro characterization of polymeric nanoparticles encapsulating plasmid DNA for gene therapy
inferred← citeshttps://doi.org/10.1080/10667857.2024.2433503openalex-snapshot
3D-printed endovascular scaffold loaded with miR-199a-5p promotes the functional repair of atherosclerosis
inferred← citeshttps://doi.org/10.1080/15257770.2025.2489495openalex-snapshot
Gene therapy and gene therapy products introduced to market by 2022
inferred← citeshttps://doi.org/10.1080/17425247.2023.2282535openalex-snapshot
Advanced approaches to overcome biological barriers in respiratory and systemic routes of administration for enhanced nucleic acid delivery to the lung
inferred← citeshttps://doi.org/10.1080/25740881.2026.2720799openalex-snapshot
Polyplex-Based Nonviral Gene Delivery: Recent Advances in Polymer Design, Mechanisms, and Therapeutic Applications
inferred← citeshttps://doi.org/10.1089/hum.2022.235openalex-snapshot
Development and Delivery of a Hands-On Short Course in Adeno-Associated Virus Manufacturing to Support Growing Workforce Needs in Gene Therapy
inferred← citeshttps://doi.org/10.1089/hum.2023.005openalex-snapshot
Chemical Epigenetic Regulation of Adeno-Associated Virus Delivered Transgenes
inferred← citeshttps://doi.org/10.1093/synbio/ysac019openalex-snapshot
Could a simple model of COVID-19 infections be the key to designing better virus-based therapies?
inferred← citeshttps://doi.org/10.1097/crd.0000000000000792openalex-snapshot
Revolutionizing Cardiac Care: The Role of Gene Therapy in Treating Cardiomyopathy
inferred← citeshttps://doi.org/10.1097/wco.0000000000001289openalex-snapshot
Gene therapies for CMT neuropathies: from the bench to the clinic
inferred← citeshttps://doi.org/10.1101/2022.08.04.502832openalex-snapshot
The Alphaherpesvirus Latency Associated Promoter 2 (LAP2) Drives Strong Transgene Expression in Peripheral Tissue Depending on Administration Route and AAV Serotype
inferred← citeshttps://doi.org/10.1101/2023.10.04.558402openalex-snapshot
Anchoring of parasitic plasmids to inactive regions of eukaryotic chromosomes through nucleosome signal
inferred← citeshttps://doi.org/10.1101/2025.07.10.660754openalex-snapshot
Preventing vision loss in a mouse model of Leber Congenital Amaurosis by engineered tRNA
inferred← citeshttps://doi.org/10.1109/biosensors65002.2025.11239295openalex-snapshot
Machine Learning-Enabled Immunosensor for Label-Free Quantification of Virus Titers
inferred← citeshttps://doi.org/10.1109/jsen.2026.3681515openalex-snapshot
Label-Free Quantification of Virus Titer Using Machine Learning-Enhanced Immunosensors
inferred← citeshttps://doi.org/10.1111/imr.13149openalex-snapshot
Gene targeting as a therapeutic avenue in diseases mediated by the complement alternative pathway
inferred← citeshttps://doi.org/10.1126/sciadv.ady6760openalex-snapshot
Liver-directed AAV gene therapy in mice corrects glycogen storage disease type IX γ2
inferred← citeshttps://doi.org/10.1128/jvi.00637-25openalex-snapshot
Retinal transduction profiling of diverse AAV serotypes via intravitreal injection
inferred← citeshttps://doi.org/10.1128/spectrum.00696-26openalex-snapshot
AdamiForge: a modular reverse genetics tool for human adenovirus type 12 (HAdV-A12)
inferred← citeshttps://doi.org/10.1134/s0006297923120179openalex-snapshot
Viral Vectors in Gene Replacement Therapy
inferred← citeshttps://doi.org/10.1134/s0026893326700172openalex-snapshot
Genes of Growth Factors and Neurotrophins as Promising Therapeutic Transgenes for Gene and Cell Therapy of Neurodegenerative Diseases
inferred← citeshttps://doi.org/10.1172/jci184929openalex-snapshot
Fgfr3 enhancer deletion markedly improves all skeletal features in a mouse model of achondroplasia
inferred← citeshttps://doi.org/10.1177/10915818251318248openalex-snapshot
Mutagenesis and Carcinogenesis Risk Evaluation for AAV and Lentiviral Gene Therapies
inferred← citeshttps://doi.org/10.1177/11206721251335560openalex-snapshot
Optogenetic therapy for retinal degenerative diseases: A review
inferred← citeshttps://doi.org/10.1186/s12951-023-02030-xopenalex-snapshot
The influence of protein corona on Graphene Oxide: implications for biomedical theranostics
inferred← citeshttps://doi.org/10.1186/s12951-026-04518-8openalex-snapshot
Gene therapy for liver diseases: methods, challenges and opportunities
inferred← citeshttps://doi.org/10.1186/s12967-022-03747-3openalex-snapshot
Current strategies employed in the manipulation of gene expression for clinical purposes
inferred← citeshttps://doi.org/10.1186/s12967-025-06392-8openalex-snapshot
Gene therapy shines light on congenital stationary night blindness for future cures
inferred← citeshttps://doi.org/10.1186/s13036-024-00404-9openalex-snapshot
An engineered ligand-responsive Csy4 endoribonuclease controls transgene expression from Sendai virus vectors
inferred← citeshttps://doi.org/10.1186/s43556-023-00160-0openalex-snapshot
Delivery of nucleic acids using nanomaterials
inferred← citeshttps://doi.org/10.1208/s12248-026-01267-2openalex-snapshot
Industry Perspective on Translational and Clinical Pharmacology Aspects of Viral-based Gene Therapies and Vaccines—Key Considerations and Learnings From Approved Products
inferred← citeshttps://doi.org/10.1208/s12249-024-03010-6openalex-snapshot
Gene Therapy: Towards a New Era of Medicine
inferred← citeshttps://doi.org/10.1515/9783111394558-015openalex-snapshot
35915 Lipid-based nanoparticles for nucleic acids delivery
inferred← citeshttps://doi.org/10.1515/psr-2025-0001openalex-snapshot
Lipid-based nanoparticles for nucleic acids delivery
inferred← citeshttps://doi.org/10.15581/10171/67875openalex-snapshot
Optimizing gene therapy for infant mice with citrullinemia type 1
showing the first 199 of 268 · page through all 268
Editorial review for independent work. ICSAC — the Institute for Complexity
Science and Advanced Computing — runs a structured editorial panel for researchers
publishing outside journals, and publishes on CiteStamp rails. Submission is free
and goes through ORCID: icsacinstitute.org/submit.